Vigeneron GmbH has received IND approval from the FDA for VG-801, a novel mRNA trans-splicing gene therapy to treat Stargardt disease and other retinal dystrophies associated with mutations in the ...
Trans-splicing is a unique process in gene expression where a short sequence, known as a spliced leader (SL), is added to the 5' end of mRNA molecules. This mechanism is particularly significant in ...
It has been proposed that isoforms of Drosophila mod(mdg4) result from the trans-splicing of independent mRNA transcripts derived from both anti-parallel DNA strands. In the August 14 Proceedings of ...
The collaboration will support development of Ascidian's RNA exon editor therapy, ACDN-01, for treating the rare genetic eye disease.
Some results have been hidden because they may be inaccessible to you
Show inaccessible results
Feedback