Satyen K. Bordoloi My first memory of cancer is the younger brother of a classmate. Blood cancer, we whispered between ...

A new gene therapy can reverse the effects of heart failure and restore heart function in a large animal model. The therapy increases the amount of blood the heart can pump and dramatically improves ...

Rocket Pharmaceuticals has shared early data from three patients that tie its gene therapy for an inherited heart disease to a well-tolerated safety profile, which has been heralded by analysts as ...

An 8-year-old boy made medical history thanks to Columbus doctors. Yet the city where it happened barely registered. Time we ...

Gene therapy is a revolutionary field in modern medicine, offering transformative potential to treat and potentially cure a wide range of genetic and acquired diseases. By addressing the root cause of ...

Forbes contributors publish independent expert analyses and insights. William A. Haseltine, Ph.D., covers genomics and regenerative medicine Today, the world stands at a crossroads in genetic medicine ...

Diseases that affect the retina, the light-sensitive layer at the back of the eye, are a significant cause of visual impairment and blindness. Gene therapy holds promise for treating some of these ...

At first glance, KJ appears to be a healthy, happy baby, but just months ago, his diagnosis of a severe metabolic disorder had his parents afraid for his life. Thanks to a multidisciplinary team of ...