This story is part of a series on the current progression in Regenerative Medicine. In 1999, I defined regenerative medicine as the collection of interventions that restore tissues and organs damaged ...

The FDA granted fast track status to VectorY’s VTx-002, an antibody gene therapy targeting TDP-43 protein aggregates in ALS.

Traditional methods for identifying therapeutic gene targets, crucial for personalized medicine, are expensive and time-consuming. While artificial intelligence (AI), particularly deep learning ...

Two of Opus's seven gene therapy assets are in clinical trials, with additional programs expected to enter the clinic.

Some gene therapy treatments use modified adeno-associated viruses (AAVs) like the one shown here to deliver therapeutic genetic material into a patient’s cells. In a finding with implications for one ...

The great hope for gene therapy is that one day it will be out of the clinic and into mainstream therapeutics. Bearing enormous potential to treat or cure disease, such technology can replace a ...

A patient death in a CRISPR trial halts gene editing studies, raising critical safety questions. What this means for the ...